Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(28 sites)
United States
Phoenix Children's Hospital, Phoenix, Arizona Children's Hospital of Orange County, Orange, California University of California, San Diego, California Yale School of Medicine, New Haven, Connecticut George Washington University School of Medicine, Washington D.C., District of Columbia Nemours Children's Health, Jacksonville, Florida University of Miami, Miami, Florida Miami Children's Hospital, Miami, Florida All Children's Hospital, St. Petersburg, Florida Children's Memorial Hospital, Chicago, Illinois Indiana University School of Medicine, Indianapolis, Indiana Children's Hospital of New Orleans, New Orleans, Louisiana Children's Mercy, Kansas City, Missouri St. Louis University, St Louis, Missouri Washington University School of Medicine (in St. Louis), St Louis, Missouri Hackensack University Medical Center, Hackensack, New Jersey Columbia University Medical Center, New York, New York University of North Carolina, Chapel Hill, North Carolina Carolinas Medical Center, Charlotte, North Carolina Duke Children's Hospital, Durham, North Carolina The University of Oklahoma, Oklahoma City, Oklahoma University of Pittsburg, Pittsburgh, Pennsylvania Cook Children's Hospital, Forth Worth, Texas Texas Transplant Institute, San Antonio, Texas University of Utah, Salt Lake City, Utah Canada
BC Children's Hospital, Vancouver, British Columbia University of Manitoba, Winnipeg, Manitoba University of Calgary, Calgary