Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(46 sites)
United States
University of Colorado Hemophilia & Thrombosis Center, Aurora, Colorado Children's National Medical Center, Washington D.C., District of Columbia University of Florida College of Medicine, Jacksonville, Florida Bleeding and Clotting Disorders Institute, Peoria, Illinois Indiana Hemophilia and Thrombosis Center, Indianapolis, Indiana University of Nebraska Medical Center, Omaha, Nebraska St. Jude Affiliate Clinic at Novant Health, Charlotte, North Carolina Comprehensive Cancer Center of Wake Forest Unversity, Winston-Salem, North Carolina Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio Rainbow Babies and Children's Hospital, Cleveland, Ohio Nationwide Children's Hospital, Columbus, Ohio Children's Hospital of Philadelphia, Philadelphia, Pennsylvania Medical University of South Carolina, Charleston, South Carolina Texas Children's Cancer and Hematology Center, Houston, Texas Texas Children's Hospital, Houston, Texas Comprehensive Center for Bleeding Disorders, Milwaukee, Wisconsin Austria
Medizinische Universität Innsbruck, Innsbruck AKH - Medizinische Universität Wien, Vienna Czechia
Fakultni nemocnice Brno, Brno France
Hôpital Morvan, Brest, Finistere Groupe Hospitalier Pellegrin - Hôpital Pellegrin, Bordeaux Groupement Hospitalier Est- Hôpital Louis Pradel, Bron CHU CAEN - Hôpital de la Côte de Nacre, Caen Groupement Hospitalier Sud - Hôpital Bicêtre, Le Kremlin-Bicêtre Hopital Cardiologique - CHU Lille, Lille CHU de Nantes Site Hotel Dieu, Nantes Hôpital Necker - Enfants Malades, Paris Germany
Universitaetsklinikum Hamburg-Eppendorf, Hamburg Werlhof-Institut GmbH, Hanover Medizinische Hochschule Hannover, Hanover Italy
Azienda Ospedaliera Universitaria Careggi, Florence Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico, Milan Azienda Ospedaliera Pediatrica Santobono Pausillipon, Naples Ospedale Pediatrico Bambino Gesù, Roma Netherlands
Erasmus Medisch Centrum, Rotterdam Russia
SBEI HPE Altai State Medical University of MoH and SD, Barnaul SAIH "Kemerovo Regional Clinical Hospital", Kemerovo FSBI of Science "Kirov Scientific and Research Institute of Hematology and Blood Transfusion of FMBA, Kirov Spain
Hospital General Universitario de Alicante, Alicante Hospital Universitari i Politecnic La Fe, Valencia Turkey (Türkiye)
Istanbul University Cerrahpasa Medical Faculty, Istanbul Ege University Medical Faculty, Izmir Ondokuz Mayis Univ. Med. Fac., Samsun Ukraine
SI Institute of Blood Pathology and Transfusion Medicine of NAMSU, Lviv United Kingdom
Royal Manchester Children's Hospital, Manchester, Greater Manchester