Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(68 sites)
United States
Children's Hospital Los Angeles, Los Angeles, California University of California at Los Angeles, Los Angeles, California Children's Hospital Colorado - Anschutz Medical Campus, Aurora, Colorado Local Institution - 2105, Orlando, Florida Local Institution - 2120, Orlando, Florida Children's Healthcare of Atlanta - Egleston Hospital, Atlanta, Georgia Maine Medical Center, Scarborough, Maine Dana Farber Cancer Institute., Boston, Massachusetts Washington University School of Medicine in St. Louis, St Louis, Missouri Local Institution - 2110, New Brunswick, New Jersey Local Institution - 2102, New York, New York Levine Children's Hospital- Pediatric Neuro-Oncology, Charlotte, North Carolina Local Institution - 2112, Cleveland, Ohio Local Institution - 2114, Hershey, Pennsylvania Children's Hospital of Philadelphia-Center for Childhood Cancer Research, Philadelphia, Pennsylvania St. Jude Children's Research Hospital, Memphis, Tennessee The University of Texas Southwestern Medical Center - Harold C Simmons Comprehensive Cancer Center, Dallas, Texas Baylor College of Medicine, Houston, Texas Local Institution - 2104, Houston, Texas Children's Hospital of Richmond at VCU, Richmond, Virginia Australia
Local Institution - 6104, Randwick, New South Wales Local Institution - 6103, Westmead, New South Wales Children's Health Queensland Hospital and Health Service, South Brisbane, Queensland Perth Childrens Hospital, Nedlands, Western Australia Canada
University Of Calgary, Calgary, Alberta Stollery Children'S Hospital, Edmonton, Alberta Children'S Hospital Of Eastern Ontario, Ottawa, Ontario St Justine Hospital, Montreal, Quebec Denmark
Rigshospitalet - Glostrup, Copenhagen France
Local Institution - 6111, Lyon, Rhone Centre Hospitalier Universitaire D'Angers, Angers Centre Hospitalier Universitaire de Bordeaux - Groupe Hospitalier Pellegrin, Bordeaux Institut d Hematologie et d Oncologie Pediatriques, Lyon Hôpitaux Universitaires de Marseille Timone, Marseille Local Institution - 6110, Marseille Local Institution - 6112, Nantes Local Institution - 6109, Paris Institut Gustave-Roussy, Villejuif Local Institution - 6108, Villejuif Italy
Fondazione IRCCS - Istituto Nazionale dei Tumori, Milan Local Institution - 6113, Padova Local Institution - 4302, Rome Local Institution - 6114, Torino Singapore
National University Hospital, Singapore KK Women's and Children's Hospital, Singapore South Korea
Local Institution - 6303, Seoul, Seodaemun-gu Seoul National University Hospital, Seoul Asan Medical Center, Seoul Local Institution - 6304, Seoul Spain
Hospital Sant Joan De Deu, Esplugues de Llobregat, Barcelona Clínica Universidad de navarra, Pamplona, Navarre Local Institution - 6105, Barcelona Hospital Universitari Vall d'Hebron, Barcelona Hospital Infantil Universitario Nino Jesus, Madrid Local Institution - 6106, Madrid Clinica Universidad de Navarra, Madrid HM Sanchinarro University Hospital, Madrid Hospital Universitario Virgen del Rocio, Seville Hospital Universitario Y Politecnico La Fe, Valencia Local Institution - 6107, Valencia Taiwan
National Taiwan University Hospital, Taipei Taipei Medical University Hospital, Taipei United Kingdom
Alder Hey Children's NHS Foundation Trust, Liverpool, England Local Institution - 4403, Birmingham University Hospital of Wales, Cardiff Royal Hosp. for Children, Glasgow The Royal Marsden NHS Foundation Trust, London Great Ormond Street Hospital For Children NHS Foundation Trust, London