Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(7 sites)
United States
University of California San Francisco, San Francisco, California Johns Hopkins, Baltimore, Maryland Washington University, St Louis, Missouri New York Medical College, Vallhala, New York Nationwide Children's Hosptial, Columbus, Ohio Children's Hospital of Pennsylvania, Philadelphia, Pennsylvania Medical College of Wisconsin, Milwaukee, Wisconsin