Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(8 sites)
United States
UCSF, Mission Bay - Benioff Children's Hospital, San Francisco, California Children's National Research Institute - Children's National Hospital, Washington D.C., District of Columbia Indiana University School of Medicine, Riley Hospital for Children, Indianapolis, Indiana University of North Carolina at Chapel Hill - North Carolina Cancer Hospital, Chapel Hill, North Carolina Atrium Health Levine Children's Hospital - Carolinas Medical Center, Charlotte, North Carolina