Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(7 sites)
United States
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois Boston Children's Hospital, Boston, Massachusetts Cincinnati Children's Hospital, Cincinnati, Ohio Children's Hospital of Philadelphia, Philadelphia, Pennsylvania The University of Texas Southwestern Medical Center, Dallas, Texas