Phase I/II Clinical Trial Stem Cell Gene Therapy in RAG1-Deficient SCID

Recruiting

Not a traditional drug trial — this study doesn't follow the standard phase structure.

Trial locations(7 sites)

Australia

The Royal Childrens Hospital, Melbourne

Italy

Ospedale Pediatrico Bambino Gesù, Roma

Netherlands

Leiden University Medical Center, Leiden

Poland

Wroclaw Medical University, Wroclaw

Spain

Hospital Universitari Vall d'Hebron, Barcelona

Turkey (Türkiye)

Erciyes Üniversitesi TIP Fakültesi, Kayseri

United Kingdom

University College London Great Ormond Street, London