Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(35 sites)
United States
Rady Children's Hospital, San Diego, California UCSF, San Francisco, California Children's Healthcare of Atlanta, Atlanta, Georgia Riley Hospital for Children at IU Health, Indianapolis, Indiana Johns Hopkins Hospital, Baltimore, Maryland Boston Children's Hospital, Boston, Massachusetts Children's Mercy Hospital and Clinics, Kansas City, Missouri Northwell Health System, New Hyde Park, New York Hassenfeld Children's Hospital at NYU Langone, New York, New York The Childrens Hospital at Montefiore Albert Einstein School of Medicine, The Bronx, New York Atrium Health Carolinas Medical, Durham, North Carolina Cincinnati Children's Hospital, Cincinnati, Ohio Oregon Health Science University School of Medicine, Portland, Oregon Monroe Carell Jr. Childrens Hospital at Vanderbilt, Nashville, Tennessee Childrens Medical Center of Dallas University of Texas Southwestern, Dallas, Texas Texas Children's Hospital, Houston, Texas Texas Liver Institute, San Antonio, Texas Australia
The Royal Children's Hospital Melbourne, Parkville, Victoria Belgium
Cliniques Universitaires Saint-Luc Bruxelles, Brussels France
Hôpital Femme Mère Enfant de Lyon, Bron Antenne pediatrique du CIC-Hopital Jeanne De Flandre, Lille Hopital Necker Enfants Malades, Paris Germany
Charité - Universitätsmedizin Berlin, Berlin Medizinische Hochschul, Hanover Universitatsklinik fur Kinder-und Jugendmedizin Tubingen, Tübingen Italy
Azienda Ospedale University, Padova Ospedale Pediatrico Bambino Gesu, Rome Malaysia
University of Malaya Medical Center, Kuala Lumpur Netherlands
Universitair Medisch Centrum Groningen, Groningen Wilhelmina Children's Hospital UMCU Utrecht, Utrecht Poland
Instytut Pomnik-Centrum Zdrowia Dzieck, Warsaw Turkey (Türkiye)
Istanbul University Istanbul Medical Faculty Hospital, Istanbul United Kingdom
Birmingham Women's and Children's NHS Foundation Trust, Birmingham King's College Hospital NHS Foundation Trust King's College Hospital Paediatric Research, London