Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(12 sites) United States
UCLA Medical Center, Los Angeles, California Lucile Packard Children's Hospital at Stanford, Palo Alto, California Altman Clinical and Translational Research Institution, San Diego, California Canada
Stollery Children's Hospital University of Alberta, Edmonton, Alberta Hospital For Sick Children, Toronto, Ontario France
Hôpital Necker - Enfants Malades APHP, Paris Netherlands
Universitair Medisch Centrum Utrecht, Utrecht Spain
Hospital Universitario Cruces, Barakaldo, Vizcaya Hospital Universitario 12 de Octubre, Madrid United Kingdom
Birmingham Children's Hospital NHS Foundation Trust, Birmingham Royal Manchester Childrens Hospital, Manchester