Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(47 sites) United States
University of Nebraska Medical Center -985400 Nebraska Medical Center, Omaha, Nebraska Cincinnati Children's Hospital Medical Center - PIN, Cincinnati, Ohio Cook Children's Health Care System, Fort Worth, Texas University of Texas MD Anderson Cancer Center - 1515 Holcombe Blvd, Houston, Texas Australia
Sydney Children's Hospital, Randwick, New South Wales Queensland Children's Hospital, South Brisbane, Queensland Royal Children's Hospital Melbourne - PIN, Parkville, Victoria Perth Children's Hospital, Nedlands, Western Australia Belgium
Hôpital Universitaire des Enfants Reine Fabiola (HUDERF), Brussels, Brussels Capital Cliniques Universitaires Saint-Luc, Woluwe-Saint-Lambert, Brussels Capital UZ Gent, Ghent, Oost-Vlaanderen Brazil
Irmandade Da Santa Casa de Misericordia de Porto Alegre, Porto Alegre, Rio Grande do Sul Hospital de Clinicas de Porto Alegre (HCPA) - PPDS, Porto Alegre, Rio Grande do Sul Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo, Porto Alegre, Rio Grande do Sul Hospital Do Rim E Hipertensão, São Paulo China
Children's Hospital Capital Institute of Pediatrics, Beijing, Beijing Municipality Beijing Children's Hospital, Capital Medical University - PIN, Beijing, Beijing Municipality Shanghai Children's Medical Center, Shanghai, Shanghai Municipality Institute of Hematology and Blood Diseases Hospital Chinese Academy of Medical Sciences - PPDS, Tianjin, Tianjin Municipality France
CHU de Rennes - Hôpital Pontchaillou, Rennes, Ille-et-Vilaine CHU de Grenoble Alpes - Hôpital Michallon, La Tronche, Isère CHRU Nantes, Nantes, Loire-Atlantique Germany
Universitätsklinikum Würzburg, Würzburg, Bavaria Universitätsklinikum Münster, Münster, North Rhine-Westphalia Universitatsklinikum Jena - Am Klinikum 1-Erlanger Allee 101, Jena, Thuringia Universitätsklinikum Hamburg Eppendorf, Hamburg Medizinische Hochschule Hannover, Hanover Israel
The Chaim Sheba Medical Center - PPDS, Ramat Gan, Tel Aviv Tel Aviv Sourasky Medical Center Ichilov - PPDS, Tel Aviv, Tel Aviv Rambam Health Care Campus - PPDS, Haifa Hadassah Medical Center- Ein Kerem - PPDS, Petah Tikva Japan
National Center for Child Health and Development, Nagoya, Aiti Saitama Children's Medical Center, Isehara-Shi, Kanagawa Shizuoka Children's Hospital, Aoi-ku, Shizuoka Hyogo Prefectural Kobe Children's Hospital, Chiba Osaka Women's and Children's Hospital, Izumi-Shi, Ôsaka Spain
Hospital Sant Joan de Deu - PIN, Espluges de Llobregat, Barcelona Hospital Universitario La Paz - PPDS, Horcajo de la Sierra, Madrid Hospital Regional Universitario de Malaga - Hospital Materno-Infantil, Málaga, Málaga Hospital Universitario Vall d´Hebron- PPDS, Barcelona Hospital Infantil Universitario Niño Jesus - PIN, Madrid United Kingdom
King's College Hospital, London, Lambeth Royal Manchester Children's Hospital - PIN, Manchester, Lancashire Nottingham University Hospitals NHS Trust, Nottingham, Nottinghamshire Birmingham Women's and Children's NHS Foundation Trust, Birmingham, West Midlands Great Ormond Street Hospital, London