A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II) — Stella
A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
Phase 2 — Testing in a larger group (up to a few hundred people) to further evaluate safety and begin to assess effectiveness.
Trial locations(32 sites)
United States
UCSF Benioff Children's Hospital Oakland, Oakland, California
Ann and Robert H Lurie Children's Hospital of Chicago, Chicago, Illinois
Hackensack University Medical Center, Hackensack, New Jersey
UNC Children's Research Institute, Chapel Hill, North Carolina
Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania
The University of Texas Medical School at Houston, Houston, Texas
University of Utah, PPDS, Salt Lake City, Utah
Argentina
Sanatorio Mater Dei, Buenos Aires
Australia
Women's and Children's Hospital, North Adelaide
Belgium
UZ Antwerpen, Antwerp, Antwerpen
Universitair Ziekenhuis Brussel, Jette, Brussels Capital
Brazil
Hospital de Clínicas de Porto Alegre (HCPA) - PPDS, Porto Alegre
Instituto Fernandes Figueira, Rio de Janeiro
Canada
University of Alberta - Faculty of Medicine & Dentistry, Edmonton, Alberta
Hospital for Sick Children, Toronto, Ontario
McGill University Health Center, Montreal, Quebec
Czechia
Vseobecna Fakultni Nemocnice V Praze, Prague
France
Hôpital Jeanne de Flandre, Lille
Germany
SphinCS, Höchheim, Hochheim
Medizinische Universität Lausitz - Carl Thiem, Cottbus
Italy
Azienda Sanitaria Universitaria Friuli Centrale - PO Universitario Santa Maria della Misericordia, Udine
Netherlands
Erasmus Medical Center - Sophia Children's Hospital, Rotterdam, Rotterdam
Spain
Hospital Universitario Vall d'Hebron, Barcelona, Barcelona
Hospital Infantil Universitario Niño Jesus, Madrid, Madrid
Sweden
Drottning Silvias Barn Och Ungdomssjukhus, Gothenburg
Turkey (Türkiye)
Cukurova University Medical Faculty Balcali Hospital, Adana
Gazi Universitesi Tip Fakultesi, Çankaya
United Kingdom
Great Ormond Street Hospital for Children, London, London
Birmingham Women's and Children's NHS Foundation Trust, Birmingham