Phase 1 â Early testing in a small group of people (usually 20â80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(7 sites)
United States
Rady Children's Hospital, San Diego, California Boston Children's Hospital, Boston, Massachusetts Nationwide Children's Hospital, Columbus, Ohio The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania The University of Utah, Salt Lake City, Utah Spain
Hospital Sant Joan de DÊu, Barcelona United Kingdom
Royal Manchester Children's Hospital, Manchester