Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(15 sites)
United States
University of California Los Angeles Medical Center, Los Angeles, California Rady Children's Hospital, San Diego, California Nemours Children s Clinic, Jacksonville, Florida Nemours Childrens Hospital, Orlando, Florida Boston Children's Hospital - Main, Boston, Massachusetts Columbia University Irving Medical Center, New York, New York Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio Seattle Children's Hospital, Seattle, Washington Medical College of Wisconsin, Milwaukee, Wisconsin Germany
University Hospital Tubingen, Tübingen Spain
Clinica Universidad de Navarra- Pamplona, Pamplona, Navarre Hospital Universitario Materno Infantil en las Palmas de Gran Canaria, Las Palmas de Gran Canaria Ramon y Cajal University Hospital, Madrid United Kingdom
Addenbrooke's Hospital, Cambridge University Hospitals NHS FT, Cambridge Great Ormond Street Hospital For Children NHS Foundation Trust, London