Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(16 sites)
United States
University of Alabama at Birmingham, Birmingham, Alabama UCSF Benioff Children's Hospital Oakland, Oakland, California Children's Hospital Colorado, Aurora, Colorado Nicklaus Children's Hospital Research Institute, Miami, Florida Rush University Medical Center, Chicago, Illinois Kennedy Krieger Institute, Baltimore, Maryland Boston Children's Hospital, Boston, Massachusetts Montefiore Medical Center, New York, New York UNC at Chapel Hill, Chapel Hill, North Carolina Nationwide Children's Hospital, Columbus, Ohio Children's Hospital of Philadelphia, Philadelphia, Pennsylvania Vanderbilt University Medical Center, Nashville, Tennessee Texas Children's Hospital, Houston, Texas Australia
The Children's Hospital at Westmead, Sydney, New South Wales United Kingdom
Royal Hospital for Children and Young People, Edinburgh Manchester University NHS Foundation Trust, Manchester