Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(65 sites)
United States
Childrens Hospital of Alabama, Birmingham, Alabama Phoenix Childrens Hospital, Phoenix, Arizona University of California, Los Angeles Interventional Clinical Trials, Los Angeles, California Nemours Hospital for Children, Wilmington, Delaware Nemours Childrens Hospital, Orlando, Florida University of South Florida - Carol and Frank Morsani Center for Advanced Health Care, Tampa, Florida Emory University, Atlanta, Georgia Indiana University, Indianapolis, Indiana Kennedy Krieger Institute, Baltimore, Maryland Boston Childrens Hospital, Boston, Massachusetts Mayo Clinic Childrens Center, Rochester, Minnesota Gillette Childrens Hospital and Clinic Saint Paul, Saint Paul, Minnesota Vanderbilt University Medical Center, Nashville, Tennessee Marshfield Clinic, Marshfield, Wisconsin Australia
Monash Childrens Hospital, Clayton, Victoria Perth Childrens Hospital, Nedlands, Western Australia Austria
Kepler Universitaetsklinikum GmbH, Linz Belgium
Universitair Ziekenhuis Leuven - Campus Gasthuisberg, Leuven Canada
Childrens Hospital of Eastern Ontario, Ottawa, Ontario The Hospital for Sick Children, Toronto, Ontario Centre Hospitalier Universitaire Sainte Justine, Montreal, Quebec China
Peking Union Medical College Hospital, Beijing, Beijing Municipality The University of Hong Kong-Shenzhen Hospital, Shenzhen, Guangdong Tongji Hospital , Tongji Medical College, Huazhong University of Science and Technology, Wuhan, Hubei Childrens Hospital of Soochow University, Suzhou, Jiangsu The First Bethune Hospital of Jilin University, Changchun, Jilin Shandong Provincial Hospital, Jinan, Shandong West China Hospital Sichuan University, Chengdu, Sichuan Shanghai Sixth Peoples Hospital, Shanghai France
Centre Hospitalier Universitaire de Bordeaux - Hopital Pellegrin, Bordeaux Centre Hospitalier Regional Universitaire de Lille, Lille Hopital Necker Enfants Malades, Paris Germany
Universitaetsklinikum Koeln, Cologne Universitaetsklinikum Wuerzburg, Würzburg Hungary
Semmelweis Egyetem, Budapest Italy
IRCCS Istituto Giannina Gaslini, Genova Centro Ricerche Cliniche Di Verona Societa responsabilita limitata, Verona Japan
Okayama Saiseikai Outpatient Center Hospital, Okayama, Okayama-ken Okayama University Hospital, Okayama, Okayama-ken Osaka Womens and Childrens Hospital, Izumi-shi, Osaka Tokyo Metropolitan Children's Medical Center, Fuchu-shi, Tokyo National Center for Child Health and Development, Setagaya-ku, Tokyo Tottori University Hospital, Yonago-shi, Tottori Poland
Centermed Krakow Sp zoo, Krakow Samodzielny Publiczny Zaklad Opieki Zdrowotnej Centralny Szpital Kliniczny UMeds, Lodz Instytut Centrum Zdrowia Matki Polki, Lodz Centrum Medyczne Medyk Spolka z Ograniczona Odpowiedzialnoscia Spolka Komandytowa, Rzeszów Szpital Miejski w Tychach Spolka z ograniczona odpowiedzialnoscia, Tychy Saudi Arabia
King Faisal Specialist Hospital and Research Centre, Riyadh Slovakia
Narodny ustav detskych chorob, Bratislava Spain
Hospital de Cruces, Barakaldo, Basque Country Hospital Universitari Vall d Hebron, Barcelona, Catalonia Hospital Sant Joan de Deu, Esplugues de Llobregat, Catalonia Hospital Universitario de Getafe, Getafe, Madrid Hospital Universitari i Politecnic La Fe, Valencia, Valencia Hospital Universitario Infantil Niño Jesus, Madrid Switzerland
Universitaets-Kinderspital beider Basel, Basel Centre Hospitalier Universitaire Vaudois, Lausanne Turkey (Türkiye)
Gazi Universitesi Saglik Arastirma ve Uygulama Merkezi Gazi Hastanesi, Ankara Marmara Universitesi Tip Fakultesi Hastanesi, Istanbul Ege Universitesi Tip Fakultesi Hastanesi, Izmir Karadeniz Teknik Universitesi Tip Fakultesi, Trabzon United Kingdom
Queen Elizabeth University Hospital, Glasgow Royal Manchester Childrens Hospital, Manchester Sheffield Childrens Hospital, Sheffield