stella
beta
A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease — Stella
Recruiting
Back to Danon Disease trials
Phase 2 — Testing in a larger group (up to a few hundred people) to further evaluate safety and begin to assess effectiveness.
Trial locations
(6 sites)
United States
University of California, San Diego, La Jolla, California
Boston Children's Hospital, Boston, Massachusetts
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania
Germany
German Heart Center Munich, Munich
Italy
Meyer Childrens Hospital, Florence
Show all 6 locations
View full record on ClinicalTrials.gov