Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy — StellaPhase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(3 sites)
United States
The University of Kansas Medical Center, Kansas City, Kansas Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio Nationwide Children's Hospital, Columbus, Ohio Last updated February 2025