Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(5 sites)
United States
Indiana University Health, Riley Hospital For Children, Indianapolis, Indiana St. Louis Children's Hospital (SLCH), St Louis, Missouri Duke University Health System, Durham, North Carolina University of Oklahoma (OU) - Medical Center - The Children's Hospital, Oklahoma City, Oklahoma The University of Texas Health Science Center at Houston (UTHSC-H) - McGovern Medical School, Houston, Texas