Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(54 sites)
United States
Santa Monica Clinical Trials, Los Angeles, California Center of Excellence in Diabetes and Endocrinology, Sacramento, California Rady Children's Hospital - Scan Diego, San Diego, California Colorado Children's Hospital, Aurora, Colorado Nemours Children's Hospital, Wilmington, Delaware Atlanta Diabetes Associates, Atlanta, Georgia Emory University School of Medicine, Atlanta, Georgia Rare Disease Research, Atlanta, Georgia Ann And Robert H Lurie Children's Hospital of Chicago, Chicago, Illinois Riley Children's Hospital, Indianapolis, Indiana Johns Hopkins Hospital, Baltimore, Maryland Mayo Clinic-PPDS, Rochester, Minnesota Maimonides Medical Center, Brooklyn, New York Montefiore Medical Center, The Bronx, New York Science 37 (at-home option), Morrisville, North Carolina CTI Clinical Research Center, Cincinnati, Ohio Center for Human Genetics, Cleveland, Ohio Texas Children's Hospital, Houston, Texas Road Runner Research, San Antonio, Texas Texas Valley Clinical Research, Weslaco, Texas Childrens Hospital of Wisconsin, Milwaukee, Wisconsin Australia
Queensland Children's Hospital, Brisbane, Queensland Royal Prince Alfred Hospital, Camperdown Sydney Children's Hospital, Randwick Children's Hospital at Westmead, Westmead Canada
AMNDX Inc., Thornhill, Ontario Jodha Tishon Inc., Toronto, Ontario Denmark
Aarhus University Hospital, Aarhus Rigshospitalet, Copenhagen France
CHU de Toulouse-Hôpital Des Enfants, Toulouse Germany
University Hospital Essen, Essen Italy
Azienda Ospedaliero Universitaria A Meyer, Florence Istituto G Gaslini Ospedale Pediatrico IRCCS - INCIPIT - PIN, Genova Ospedale San Raffaele S.r.l. - PPDS, Milan Azienda Ospedale Università Padova - Dipartimento Salute della Donna e del Bambino - INCIPIT - PIN, Padova Ospedale Pediatrico Bambino Gesù IRCCS, Roma IRCCS Materno Infantile Burlo Garofolo - INCIPIT - PIN, Trieste Poland
Samodzielny Publiczny Szpital Kliniczny, Szczecin Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wroclawiu-Chalubinskiego 2-2a, Wroclaw Romania
Institutul National de Endocrinologie C. I. Parhon, Bucharest Institutul National de Endocrinologie C. I. Parhon, Bucharest National Clinical Center for Children Neurorehabilitation "Dr. Nicolae Robanescu", Bucharest Louis Turcanu Emergency Clinical Hospital for Children, Timișoara Spain
Corporacio Sanitaria Parc Tauli, Sabadell, Barcelona Hospital Sant Joan de Deu, Barcelona Hospital Universitario 12 de Octubre, Madrid Universitario Virgen de la Victoria, Málaga Sweden
Karolinska Universitetssjukhuset Solna, Solna United Kingdom
Fulbourn Hospital, Cambridge, England Hull Royal Infirmary, Hull, England Ninewells Hospital - PPDS, Dundee, Scotland Royal Hospital for Children and Young People, Edinburgh, Scotland