Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(21 sites)
United States
University of Alabama/Children's of Alabama, Birmingham, Alabama Phoenix Children's Hospital, Phoenix, Arizona UCSF Benioff Children's Hospital Oakland, Oakland, California Rady Children's Hospital, San Diego, California University of Florida, Gainesville, Florida