Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(7 sites)
United States
Cedars-Sinai Medical Center, Los Angeles, California University of California, San Francisco, San Francisco, California Boston Children's Hospital, Boston, Massachusetts Dana-Farber Cancer Institute, Boston, Massachusetts Children's Hospital of Philadelphia, Philadelphia, Pennsylvania Texas Children's Hospital, Houston, Texas University of Utah Hospital, Salt Lake City, Utah