Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(9 sites)
United States
University of California, Los Angeles, Los Angeles, California University of California, San Francisco, San Francisco, California Johns Hopkins All Children's Hospital, St. Petersburg, Florida Boston Children's Hospital, Boston, Massachusetts University of Minnesota, Minneapolis, Minnesota Columbia University Irving Medical Center, Morgan Stanley Children's Hospital, New York, New York Duke University, Durham, North Carolina University of Utah, Primary Children's Hospital, Salt Lake City, Utah United Kingdom
University College London Hospital, London