Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.

Trial locations(14 sites)

United States

UCSF Wayne and Gladys Valley Center for Vision, San Francisco, California

University of Miami - Bascom Palmer Eye Institute, Miami, Florida

University of Iowa, Iowa City, Iowa

University of Minnesota Medical School, Minneapolis, Minnesota

University of Pennsylvania - Center for Advanced Retinal & Ocular Therapeutics, Philadelphia, Pennsylvania

Belgium

Universitair Ziekenhuis Gent (UZ), Ghent

Canada

University of Alberta, Edmonton, Alberta

The Hospital for Sick Children - SickKids, Toronto, Ontario

France

Centre de maladies rares CHNO des Quinze Vingt, Paris

Germany

Justus-Liebig Universität - Department of Ophthalmology, Giessen

Klinikum der Ludwig-Maximilian Universität München, München

University of Tuebingen - Inst. for Ophthalmic Research, Tübingen

Netherlands

Radboud Universitair Medisch Centrum, Nijmegen

United Kingdom

Moorfields Eye Hospital NHS Foundation Trust, London