Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(4 sites)
United States
University of California at San Diego - Rady Children's Hospital, San Diego, California Stanford University - Stanford Children's Health, Stanford, California Emory University School of Medicine - Children's Healthcare of Atlanta (recuiting Cohort 0), Atlanta, Georgia Baylor College of Medicine - Texas Children's Hospital (recuiting Cohort 0), Houston, Texas