Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
(34 sites) United States
UCLA Neurology Outpatient Clinic at Westwood, Los Angeles, California Norman Fixel Institute for Neurological Diseases UF Health, Gainesville, Florida USF Health Morsani College of Medicine Department of Neurology, Tampa, Florida Children's Hospital of Philadelphia - Buerger Center for Advanced Pediatric Care - PIN, Philadelphia, Pennsylvania St. Jude Children's Research Hospital - PIN, Memphis, Tennessee CHKD's Health Center - South Campus - PIN, Norfolk, Virginia Seattle Children's Hospital, Seattle, Washington Australia
Sydney Children's Hospital, Randwick, New South Wales Murdoch Childrens Research Institute (MCRI), Parkville, Victoria Austria
Universitätsklinikum Innsbruck, Innsbruck Brazil
L2 Ip - Instituto de Pesquisas Clinicas Ltda - ME, Brasília, Federal District University of Campinas (UNICAMP) School of Medical Sciences, Campinas, São Paulo PSEG Centro de Pesquisa Clinica, São Paulo, São Paulo Canada
McGill University, Montreal, Quebec CHU de Quebec -Universite Laval, Québec, Quebec Denmark
Rigshospitalet - Juliane Marie Centret (JMC) Copenhagen, Copenhagen France
CHU de Montpellier- Hôpital Gui De Chauliac, Montpellier, Hérault AP-HP - Hôpital Armand Trousseau, Paris Germany
Universitätsklinikum Aachen, Aachen, North Rhine-Westphalia UKGM - Universitätsklinikum Giessen und Marburg GmbH - Standort Gießen, Giessen Universitätsklinikum Hamburg Eppendorf, Hamburg India
All India Institute of Medical Sciences (AIIMS) - New Delhi, New Delhi, National Capital Territory of Delhi Ireland
CHI at Temple Street, Dublin Italy
Ospedale Pediatrico Bambino Gesù IRCCS, Rome, Lazio IRCCS Eugenio Medea - Polo. Scientifico Veneto, Conegliano, Veneto Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan Netherlands
Radboud Universitair Medisch Centrum, Nijmegen Saudi Arabia
King Faisal Specialist Hospital & Research Centre, Riyadh, Ar Riya Spain
Hospital Sant Joan de Deu - PIN, Espluges de Llobregat, Barcelona Hospital Universitario La Paz - PPDS, Madrid Turkey (Türkiye)
Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi, Istanbul United Kingdom
University College Hospital - PPDS, London, Lincolnshire John Radcliffe Hospital, Oxford, Oxfordshire Sheffield Children's Hospital - PPDS, Sheffield, South Yorkshire