Plain-English translation of NCT04000165 on ClinicalTrials.gov โ ยท Source last updated ยท How we translate trials
Read our Sickle cell disease research guide โPhase 1 โ Testing in a small group (usually 20โ80 people) to find a safe dose and watch for side effects.
United States
Phase
Safety & dosing
Sponsor
National Institutes of Health Clinical Center (CC)
Collaborators
National Heart, Lung, and Blood Institute (NHLBI), Agios Pharmaceuticals, Inc.
Enrollment target
~17 participants
Started
July 2019
Primary completion
June 2021
Age range
18 Years โ 70 Years
Last updated on clinicaltrials.gov in July 2022.