Plain-English translation of NCT04509050 on ClinicalTrials.gov ↗ · Source last updated · Translation generated · How we translate trials
Read our Cystic Fibrosis research guide →This study is following young children with cystic fibrosis to understand how new medications like affect their bodies and health. Researchers want to learn whether this medication helps children grow better, breathe easier, and improve their digestion and other body functions over a long period of time.
Cystic fibrosis is a serious genetic condition that affects the lungs and digestion. These new medications work differently and more powerfully than older treatments, but doctors need to understand exactly how they change a child's health, growth, and development over time so they can help children thrive.
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You and your child would visit the research clinic multiple times over up to 5 years (Part A) or up to 5 years after starting the medication (Part B). At each visit, researchers would do routine tests like measuring your child's height and weight, checking lung function, and taking blood or stool samples to track growth hormones, digestion, and overall health. There are no experimental medicines given during this study—doctors only observe how the medication your child's doctor prescribes works in real life.
AI-generated summary from trial data · Jun 3, 2026 · Not medical advice
United States