Plain-English translation of NCT04626674 on ClinicalTrials.gov ↗ · Source last updated · How we translate trials
Read our Duchenne Muscular Dystrophy research guide →Phase 1 — Testing in a small group (usually 20–80 people) to find a safe dose and watch for side effects.
United States
2 Years and older
Sex
Male only
Last updated on clinicaltrials.gov in June 2026.
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Central contact
Sarepta Therapeutics Inc., For Clinical Trial Information, Select Option 4
Sarepta Therapeutics, Inc.
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