Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(10 sites)
United States
UCSF Benioff Children's Hospitals, San Francisco, California Colorado Children's Hospital, Aurora, Colorado Nicklaus Children's Hospital, Miami, Florida Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois Boston Children's Hospital, Boston, Massachusetts Oregon Health and Science University (OSHU), Portland, Oregon Cook Children's Medical Center, Fort Worth, Texas Australia
The Royal Children's Hospital, Melbourne United Kingdom
Queen Elizabeth Hospital, Glasgow Great Ormond Street Hospital, London