Efficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease

Recruiting

Phase 2 — Testing in a larger group (up to a few hundred people) to further evaluate safety and begin to assess effectiveness.

Trial locations(35 sites)

United States

University of California, Irvine - ALS & Neuromuscular Center, Orange, California

The Regents of the University of California - San Diego, San Diego, California

Children's Hospital Colorado - Center for Cancer and Blood Disorders (CCBD) - Anschutz Medical Campus Location, Aurora, Colorado

Rare Disease Research, LLC, Atlanta, Georgia

Mayo Clinic, Rochester, Minnesota

Washington University School of Medicine - Center for Advanced Medicine (CAM) - Neuroscience Center, St Louis, Missouri

Columbia University Irving Medical Center, New York, New York

Akron Children's Hospital, Akron, Ohio

UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania

Baylor College of Medicine (BCM), Houston, Texas

The University of Texas Health Science Center at Houston, Houston, Texas

Belgium

Hopital Universitaire de Bruxelles (H.U.B)/ Academisch Ziekenhuis Brussel, Brussels

Universitair Ziekenhuis Gent, Ghent

Universitair Ziekenhuis Leuven Gasthuisberg Campus, Leuven

Denmark

Copenhagen Neuromuscular Center, Rigshospitalet, Copenhagen

France

Centre Hospitalier Universitaire (CHU) de Bordeaux - Groupe Hospitalier Pellegrin, Bordeaux

Hopital Roger Salengro, CHRU de Lille, Lille

Centre Hospitalier Universitaire de Nice, Hopital Pasteur 2, Nice

CHU de NICE - Hôpital Archet 2, Nice

Groupe Hospitalier Pitie-Salpetriere, Paris

Germany

Charite - Universitaetsmedizin Berlin, Berlin

Universitaetsklinikum Halle, Halle

Italy

IRCCS Institute of Neurological Sciences of Bologna- Universita di Bologna, Bologna

Azienda Ospedaliera Universitaria Gaetano Martino Messina, Messina

Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan

Azienda Ospedaliero Universitaria Pisana, Pisa

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Universita Cattolica del Sacro Cuore, Roma

Netherlands

Radboud University Medical Center, Nijmegen

Spain

CIBERER- IDIBAPS, Faculty of Medicine, University of Barcelona, Barcelona

Hospital de la Santa Creu i Sant Pau, Barcelona

Hospital General Universitario de Catalunya, Barcelona

Hospital Universitario 12 de Octubre, Madrid

United Kingdom

Department of Clinical Neurosciences, Addenbrooke's Hospital, Cambridge

University College London Hospitals Nhs Foundation Trust, London

Royal Victoria Infirmary - The Newcastle Upon Tyne Hospitals NHS Foundation Trust, Newcastle