Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(9 sites)
United States
University of California, San Francisco Benioff Children's Hospital, San Francisco, California University of Iowa, Iowa City, Iowa Boston Children's Hospital, Boston, Massachusetts Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio Children's Hospital of Philadelphia, Philadelphia, Pennsylvania Vanderbilt Bill Wilkerson Center, Nashville, Tennessee Canada
The Hospital for Sick Children Jaina.negandhi@sickkids.ca +1 (416) 813 6683, Toronto, Ontario Taiwan
National Taiwan University Hospital, Taipei United Kingdom
University College London, London, United Kingdom