Plain-English translation of NCT06151600 on ClinicalTrials.gov ↗ · Source last updated · Translation generated · How we translate trials
This is a observational study that follows people diagnosed with CMT4J, a rare inherited nerve disease that affects how nerves communicate with muscles. Researchers will not test a new medication, but instead will track participants over time with regular medical exams, nerve tests, and imaging to understand how the disease develops and progresses.
Very little is known about how CMT4J changes over time in different people. By carefully following patients and collecting detailed information, researchers hope to better understand the disease's natural course and develop better tools to measure how treatments might help in the future.
You will visit the study center once a year for up to 2 years. At each visit, you'll have a physical and nerve exam, standard blood tests, imaging scans (like muscle MRI), nerve conduction studies, and possibly lung function tests. The study is purely observational—no medication is being tested—so you'll simply be monitored to help researchers understand how your condition changes naturally over time.
AI-generated summary from trial data · Jul 11, 2026 · Not medical advice
United States
Sponsor
Elpida Therapeutics SPC
Enrollment target
~20 participants
Started
July 2024
Primary completion
March 2031
Last updated on clinicaltrials.gov in July 2026.