Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(10 sites)
United States
Rady Children's Hospital, San Diego, California Children's Hospital Colorado, Aurora, Colorado Children's Healthcare of Atlanta, Atlanta, Georgia Children's Mercy Hospital of Kansas City, Kansas City, Missouri Memorial Sloan- Kettering Cancer Center, New York, New York