Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(103 sites)
United States
Univ of Alabama Birmingham, Birmingham, Alabama Phoenix Children's Hsptl, Phoenix, Arizona Children's Hospital Los Angeles - Endocrinology, Los Angeles, California Children's Hospital Los Angeles - Endocrinology, Los Angeles, California UCSF Oakland Benioff ChildHosp, Oakland, California UCSF Oakland Benioff ChildHosp, Oakland, California Children's Hosp Of Orange, Orange, California University Of California Irvine, Orange, California University of Connecticut, Farmington, Connecticut Children's National Medical Center, Washington D.C., District of Columbia Foundation for Sickle Cell Disease Research, Hollywood, Florida Univ of Miami/SCCC, Miami, Florida Emory University School of Medicine, Atlanta, Georgia Children's Healthcare Atlanta, Atlanta, Georgia Center for Blood Disorders Augusta University, Augusta, Georgia Univer Of Illinois at Chicago, Chicago, Illinois Children's Hosp-New Orleans, New Orleans, Louisiana Boston Medical Center, Boston, Massachusetts Washington University-St.Louis, St Louis, Missouri NYC Health+Hospitals, Brooklyn, New York Columbia University Medical Center_New York_0, New York, New York Columbia University Medical Center_New York_0, New York, New York Weill Cornell Med Coll-NYPH, New York, New York Jacobi Medical Center, The Bronx, New York Montefiore Medical Center, The Bronx, New York Atrium Levine Children's/Atrium Health, Charlotte, North Carolina Duke University_Durham, Durham, North Carolina East Carolina Univ-Greenville, Greenville, North Carolina East Carolina University_Greenville, Greenville, North Carolina Atrium Health-Wake Forest Bapt, Winston-Salem, North Carolina Cincinnati Child's Hsp Med Ctr, Cincinnati, Ohio Neuro-Behavioral Clinical Research, North Canton, Ohio Medical University Of South Carolina_Charleston, Charleston, South Carolina Methodist University Hospital, Memphis, Tennessee Texas Children's Hospital_Houston, Houston, Texas UT Health University of Texas, Houston, Texas Virginia Comm Univ Medical Ctr, Richmond, Virginia Mary Bridge Children's Health, Tacoma, Washington Versiti, CCBD_Milwaukee, Milwaukee, Wisconsin Canada
St Pauls Hospital, Vancouver, British Columbia The Hospital for Sick Children, Toronto, Ontario University Health Network - Toronto General Hospital, Toronto, Ontario CHU Ste-Justine, Montreal, Quebec Egypt
Alexandria University Hospital, Alexandria, Egypt Zagazig University Hospital, Alsharkia, Egypt Faculty of Medicine Ain Shams Medical Research Institute (MASRI), Cairo Cairo University, Cairo, Egypt Abu El-Reesh El-Mounira Children University Hospital, Cairo, Egypt France
Ap-Hp-Hopital Henri Mondor, Créteil Hospices Civils de Lyon-Hopital Edouard Herriot, Lyon Ap-Hp-Hopital Robert Debre, Paris Ap-Hp-Hopital Robert Debre, Paris Germany
Charité - Campus Virchow-Klinikum - Klinik für Pädiatrie mit Schwerpunkt Onkologie und Hämatologie, Berlin Universitätsklinikum Freiburg - Kinder- und Jugendklinik, Freiburg im Breisgau Ghana
Kintampo Health Research Centre (KHRC), Kintampo, Bono East Ghana Institute of Clinical Genetics, Korle Bu Teaching Hospital (KBTH), Accra Greece
General Hospital Of Larissa Koutlibaneio And Triantafylleio - Thalassemia and SCD Unit, Larissa, Thessaly Hippokration Hospital, Athens General University Hospital of Patras, Pátrai 'Ippokrateio' General Hospital of Thessaloniki, Thessaloniki India
All India Institute of Medical Sciences (AIIMS), Raipur, Raipur, Chhattisgarh K.J Somaiya Hospital and Research Centre, Mumbai, Maharashtra Victoria Hospital, Bangalore, Bangalore Nirmal Hospital Pvt. Ltd., Gujarat Suretech Hospital and Research Centre Ltd., Maharashtra All India Institute of Medical Sciences_Delhi, New Delhi Italy
Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche, Orbassano, Torino Azienda Ospedale Universita Padova, Padova Fondazione IRCCS Policlinico San Matteo, Pavia Kenya
Gertrude's Children's Hospital, Nairobi, Nairobi County KEMRI CRDR Siaya Clinical Research Annex, Country Referral Hospital, Siaya, Siaya County KEMRI-Walter-Reed Kericho, Kericho Kombewa Clinical Research Centre, Kisumu KEMRI Kondele Children Hospital, Kisumu, Kisumu Ahero Clinical Trials Unit, Kisumu Lebanon
American University of Beirut Medical Centre, Hamra Chronic Care Center, Hazmiyeh Nigeria
University of Nigeria Teaching Hospital (UNTH), Ituku-Ozalla, Enugu State University College Hospital Paediatric Haematology and Oncology Unit, Ibadan, Ibadan, Oyo State University of Abuja Teaching Hospital, Gwagwalada, Abuja, Abuja Barau Dikko Teaching Hospital, Kaduna, Kaduna Aminu Kano Teaching Hospital (AKTH), Kano Lagos University Teaching Hospital, Lagos, Lagos Oman
Sultan Qaboos University Hospital, Muscat, Sultanet of Oman/Muscat/Al Khoud Saudi Arabia
Prince Mohammad Bin Naser Hospital, Jizan King Khalid University Hospital, Riyadh Spain
Hospital Universitario de Cruces, Barakaldo Hospital Vall d'Hebron, Barcelona Hospital Universitario La Paz, Madrid Turkey (Türkiye)
Baskent Universitesi Adana, Adana Başkent Üniversitesi Adana-Hematoloji, Adana Hacettepe University Hematology, Ankara Hacettepe Üniversitesi Hastanesi- Hematoloji, Ankara Mersin University Medical Faculty Pediatric Hematology, Mersin Mersin Üniversitesi Tip Fakültesi Hastanesi- Çiftlikköy Yerleşkesi- Hematoloji, Mersin United Kingdom
Guy's Hospital - Haematology, London King's College Hospital - Paediatric Research, London Kings College Hospital - Haematology, London Imperial College London, London Manchester Royal Infirmary, Manchester Royal Hallamshire Hospital, Sheffield