Phase 1 — Early testing in a small group of people (usually 20–80) to evaluate safety, determine safe dosage, and identify side effects.
Trial locations(4 sites)
United States
Orthopaedic Institute for Children/Orthopaedic Hemophilia Treatment Center, Los Angeles, California India
Nirmal Hospital Pvt Ltd., Surat, Gujarat K J Somaiya Hospital & Research Centre, Mumbai, Maharashtra Turkey (Türkiye)
Ege University Faculty of Medicine Dean's Office, Bornova, İzmir