Phase 3 — Large-scale testing across thousands of people, comparing the new treatment against current standard treatments.
Trial locations(61 sites)
United States
Phoenix Children's Hospital, Phoenix, Arizona Arkansas Children's Hospital, Little Rock, Arkansas Cedars Sinai Medical Center, Los Angeles, California Children's Hospital of Orange County, Orange, California USCF Medical Center, San Francisco, California Children's Hospital Colorado, Aurora, Colorado Children's National Medical Center, Washington D.C., District of Columbia Nemours Children's Health, Jacksonville, Florida Nicklaus Children's Hospital, Miami, Florida Advent Health Neuroscience Research Institute, Orlando, Florida Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois University of Iowa Hospital and Clinics, Iowa City, Iowa Massachusetts General Hospital, Boston, Massachusetts Boston Children's Hospital, Boston, Massachusetts CS Mott Children's Hospital, Ann Arbor, Michigan Mayo Clinic, Rochester, Minnesota Washington University in St. Louis School of Medicine, St Louis, Missouri NYU Langone Health, New York, New York Weill Cornell Medicine, New York, New York University of Rochester Medical Center, Rochester, New York University of North Carolina at Chapel Hill, Chapel Hill, North Carolina Duke University Health System, Durham, North Carolina Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio Cleveland Clinic, Cleveland, Ohio Nationwide Children's Hospital, Columbus, Ohio Oregon Health & Science University (OHSU), Portland, Oregon LeBonheur Children's Hospital, Memphis, Tennessee Cook Children's Medical Center, Fort Worth, Texas Texas Children's Hospital, Houston, Texas University of Utah Primary Children's Hospital, Salt Lake City, Utah UVA Health, Charlottesville, Virginia France
Hôpital de la Timone, Marseille Hôpital Necker - Enfants Malades, Paris Hôpital Robert Debré - Paris, Paris Germany
Charité - Campus Virchow-Klinikum, Berlin Universitaetsklinikum Bonn AoeR, Bonn Universitaetsklinikum Frankfurt Goethe-Universitaet, Frankfurt Universitaetsklinikum Freiburg, Friedberg Universitaetsklinikum Heidelberg, Heidelberg Integriertes Sozialpaediatrisches Zentrum, München Italy
Azienda Ospedaliero Universitaria Ospedale Pediatrico Meyer, Florence Istituto Giannina Gaslini-Ospedale Pediatrico IRCCS, Genova Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma Ospedale Pediatrico Bambino Gesù, Roma Japan
Fukuoka Children's Hospital, Fukuoka Hokkaido University Hospital, Hokkaido Kyoto University Hospital, Kyoto Nagoya University Hospital, Nagoya National Hospital Organization Nishi Niigata Central Hospital, Niigata Okayama University Hospital, Okayama Osaka City General Hospital, Osaka Jichi Medical University Hospital, Shimotsuke National Center of Neurology and Psychiatry, Tokyo Yokohama City University Medical Center, Yokohama Spain
Hospital Blua Sanitas Valdebebas, Madrid Hospital Ruber Internacional, Madrid Clinica Universidad de Navarra, Pamplona United Kingdom
Royal Hospital for Children, Glasgow Great Ormond Street Hospital for Children, London Sheffield Children's Hospital, Sheffield