Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Recruiting

Phase 2 — Testing in a larger group (up to a few hundred people) to further evaluate safety and begin to assess effectiveness.

Trial locations(28 sites)

United States

University of California - Irvine Medical Center, Irvine, California

University of Florida (UF) - Gainesville, Gainesville, Florida

Emory University Hospital, Atlanta, Georgia

Washington University in St. Louis, St Louis, Missouri

Duke University Medical Center, Durham, North Carolina